Removing Barriers Between Patients and Life-Changing Treatments
For patients with rare diseases, access can be the single most critical component of care. Aegerion provides a range of programs and services designed to reduce delays, improve adherence, and help patients and families navigate the healthcare system.
Patient Access & Support Programs
Our access and support services include:
Named-patient and early-access programs for pre-approval treatment
Compassionate use programs where approved therapies are not otherwise available
Insurance and reimbursement support in collaboration with payers and providers
Education and adherence initiatives tailored to complex conditions
We believe access is not just about availability — it’s about support, affordability, and empowerment.
Patient Access & Support Programs
Empowering Patients. Supporting Journeys. Ensuring Access.
At Aegerion Pharmaceuticals UK, we recognize that receiving a diagnosis for a rare disease is only the beginning of a complex journey. Our Patient Access & Support Programs are designed to ensure that patients—and the healthcare professionals who care for them—have the guidance, tools, and resources needed to access and continue treatment with confidence.
Because when it comes to rare diseases, every patient matters and every step counts.
A Holistic Support Model
Our approach goes beyond simply providing treatment. We offer comprehensive, personalized support to address the full spectrum of patient needs—medical, emotional, financial, and logistical.
1. Access to Therapy
Navigating the healthcare system and reimbursement processes can be overwhelming—especially with high-cost, specialized therapies. We help ease that burden through:
Dedicated access specialists who work with NHS services and private insurers
Support with prior authorisations and reimbursement submissions
Financial assistance programs (where applicable) to reduce out-of-pocket costs
Guidance on named patient or early access programs
2. Personalized Patient Support
We understand that rare diseases affect individuals and families in profoundly personal ways. That’s why our programs offer tailored patient support, including:
Nurse case managers who provide 1:1 support and education
Ongoing treatment adherence guidance
Help with managing treatment schedules, side effects, and lifestyle changes
Emotional support services or referrals through advocacy partnerships
3. Education and Empowerment
Empowering patients and caregivers with knowledge leads to better outcomes. Aegerion provides:
Disease and treatment education materials for patients, families, and carers
Workshops, webinars, and helplines to keep patients informed and engaged
Resources in multiple formats (digital, print, and in-clinic) for accessibility
Support for Healthcare Professionals
We also support the physicians, nurses, and pharmacists involved in rare disease care. Our clinical support services include:
Specialist medical information and training
Assistance with diagnostic tools and patient identification
Updates on treatment protocols and real-world data insights
Collaborative care planning tools to streamline multidisciplinary support
A Long-Term Commitment
Aegerion’s Patient Access & Support Programs are not “one-size-fits-all” and not limited to the initial prescription. We are committed to long-term engagement, ensuring patients remain supported throughout their treatment journey.
Our teams monitor patient feedback and collaborate with healthcare providers to continuously improve the program’s reach, responsiveness, and relevance.
Our Promise to Patients
We believe that no patient should be left behind due to where they live, what they can afford, or how rare their condition is. At Aegerion Pharmaceuticals UK, we work every day to turn access into action—so that patients not only receive life-changing treatment but experience lasting support.
If you are a patient, caregiver, or healthcare provider looking for support, our Access & Support Team is here to help. Contact Us
Orphan Drug Commercialization
Helping Breakthrough Therapies Reach Those Who Need Them Most
Aegerion Pharmaceuticals UK specializes in the regulatory, operational, and strategic processes required to commercialize orphan and ultra-orphan therapies in the UK and across the European market. Our deep understanding of the rare disease landscape enables us to navigate the unique challenges of small patient populations, complex clinical data, and strict approval frameworks.
